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Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder
Journal article   Peer reviewed

Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder

A. A. Lau, T. Rozaklis, S. Ibanes, A. J. Luck, H. Beard, S. Hassiotis, K. Mazouni, J. J. Hopwood, E. J. Kremer and K. M. Hemsley
Gene, Vol.491(1), pp.53--7
2012

Abstract

Canine/*genetics Animals Brain/metabolism Cells Cultured Gene Transfer Techniques Genetic Therapy Genetic Vectors Helper Viruses/genetics Hydrolases/*genetics Mucopolysaccharidosis III/*therapy Transgenes Adenoviruses
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