- Title
- Gathering real-world compassionate data to expand eligibility for elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with N1303K or other rare CFTR variants: a viewpoint
- Creators - without role
- Pierre-Régis BurgelIsabelle Sermet-Gaudelus - Institut Necker Enfants MaladesEmmanuelle Girodon - Hôpital CochinReem Kanaan - Assistance Publique – Hôpitaux de ParisJean Le Bihan - ManRos TherapeuticsNatascha Remus - Hôpital Intercommunal de CréteilBruno Ravoninjatovo - Université de Reims Champagne-ArdenneDominique Grenet - Hôpital FochMichele Porzio - Université de StrasbourgVéronique Houdouin - Hôpital Robert-DebréLaurence Le Clainche-Viala - Hôpital Robert-DebréIsabelle Durieu - Hospices Civils de LyonRaphaele Nove-Josserand - Hospices Civils de LyonJeanne Languepin - Centre Hospitalier Universitaire de LimogesBérangère Coltey - Hôpital NordAnne Guillaumot - Université de LorraineCamille Audousset - Centre Hospitalier Universitaire de LilleRaphaël Chiron - Université de Montpellier, Hydrosciences Montpellier - HSMLaurence Weiss - Hôpital d'HautepierreIsabelle Fajac - Hôpital CochinJennifer da Silva - Assistance Publique – Hôpitaux de ParisClémence Martin - Cystic Fibrosis Foundation
- Publication Details
- European Respiratory Journal, Vol.63(1)
- Identifiers
- 9941386109311
- Academic Unit
- Hydrosciences Montpellier - HSM
- Language
- English
- Resource Type
- Journal article
- Local Fields
- hal-04930869
Journal article
Gathering real-world compassionate data to expand eligibility for elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with N1303K or other rare CFTR variants: a viewpoint
European Respiratory Journal, Vol.63(1)
19/01/2024
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