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Clinically Distinct Phenotypes of Canavan Disease Correlate with Residual Aspartoacylase Enzyme Activity
Journal article   Open access   Peer reviewed

Clinically Distinct Phenotypes of Canavan Disease Correlate with Residual Aspartoacylase Enzyme Activity

Marisa Mendes, Desirée Ec Smith, Ana Pop, Pascal Lennertz, Matilde Fernandez Ojeda, Warsha Kanhai, Silvy Jm van Dooren, Yair Anikster, Ivo Barić, Caroline Boelen, …
Human Mutation, Vol.38(5), pp.524 - 531
05/2017
PMCID: PMC5412892
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https://doi.org/10.1002/humu.23181View
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