- Titre
- Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database
- Créateurs - sans rôle
- Zaïda Koeks - Leiden University Medical CenterCatherine Bladen - Muscular Dystrophy UKEn SalgadoErik van Zwet - Leiden University Medical CenterOksana Pogoryelova - Muscular Dystrophy UKGrace Mcmacken - Muscular Dystrophy UKSoledad Monges - Garrahan HospitalMaria Foncuberta - Garrahan HospitalKyriaki Kekou - National and Kapodistrian University of AthensKonstantina Kosma - National and Kapodistrian University of AthensHugh Dawkins - Government of Western Australia Department of HealthLeanne Lamont - Government of Western Australia Department of HealthMatthew M. Bellgard - Murdoch UniversityAnn RoyTeodora Chamova - Medical University of SofiaVelina Guergueltcheva - Medical University of SofiaSophelia ChanLawrence Korngut - University of CalgaryCraig Campbell - Western UniversityYi Dai - Chinese Academy of Medical Sciences & Peking Union Medical CollegeJen WangNina Barišić - University of ZagrebPetr Brabec - Masaryk UniversityJaana Lähdetie - Turku University HospitalMaggie C. Walter - Ludwig-Maximilians-Universität MünchenOlivia Schreiber-Katz - Ludwig-Maximilians-Universität MünchenVeronika KarcagiMarta GaramiAgnes Herczegfalvi - Semmelweis UniversityVenkatarman Viswanathan - Kanchi Kamakoti CHILDS Trust HospitalFarhad Bayat - Pasteur Institute of IranFilippo Buccella - Parent Project OnlusAlessandra Ferlini - University of FerraraEn KimuraJan van den Bergen - Leiden University Medical CenterMiriam Rodrigues - Auckland District Health BoardRichard Roxburgh - Auckland District Health BoardAnn LusakowskaAnn Kostera-PruszczykRosário Santos - Centro de Genética ClínicaElena NeaguSvetlana Artemieva - Scientific Center of Children's HealthVedrana Milic Rasic - University Children's Hospital, BelgradeDina Vojinovic - Erasmus University RotterdamManuel Posada - MedicinaClemens Bloetzer - Institute of Social and Preventive MedicineAndrea Klein - University of LausanneJordi Díaz-Manera - Hospital de Sant PauEduard Gallardo - University of LausanneA. Ayşe Karaduman - Hacettepe UniversityTunca Oznur - Hacettepe UniversityHaluk Topaloğlu - Hacettepe UniversityRasha El Sherif - Ain Shams University HospitalAngela StringerAndriy Shatillo - Institute of Neurology, Psychiatry and NarcologyAnn MartinHolly PeayJan KirschnerKevin Flanigan - Nationwide Children's HospitalVolker Straub - Muscular Dystrophy UKKate Bushby - Muscular Dystrophy UKChristophe Béroud - Université de Montpellier, Institut de Génétique Humaine - IGHJan VerschuurenHanns Lochmuller - Muscular Dystrophy UK
- Détails de publication
- Journal of Neuromuscular Diseases, Vol.4(4), pp.293 - 306
- Identifiants
- 99161161209311
- Unité académique
- Institut de Génétique Humaine - IGH
- Langue
- English
- Type de ressource
- Journal article
- Champs locaux
- hal-01779991
Article de revue
Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database
Journal of Neuromuscular Diseases, Vol.4(4), pp.293 - 306
21/11/2017
PMCID: PMC5701764
Indicateurs
1 Consultations de la notice